SMN IMMUNOGENE THERAPY FOR MOTOR NEURON DISORDERS

Grant number: 1104299 | Funding period: 2016 - 2018

Completed

Abstract

We have designed novel gene therapy agents to treat MND. This therapeutic approach uniquely combines gene therapy agents with antibodies which stimulate motor neuron health and connections to muscle. This project will comprehensively characterise the therapeutic effects of our novel gene therapy agents in MND mice. We predict that our gene therapy complexes will improve motor neuron survival,motor function and lifespan in MND mice.

Related publications (10)

Researchers