Journal article
Efficacy and safety of cyclic pyranopterin monophosphate substitution in severe molybdenum cofactor deficiency type A: a prospective cohort study
Bernd C Schwahn, Francjan J Van Spronsen, Abdel A Belaidi, Stephen Bowhay, John Christodoulou, Terry G Derks, Julia B Hennermann, Elisabeth Jameson, Kai Koenig, Tracy L McGregor, Esperanza Font-Montgomery, Jose A Santamaria-Araujo, Saikat Santra, Mamta Vaidya, Anne Vierzig, Evangeline Wassmer, Ilona Weis, Flora Y Wong, Alex Veldman, Guenter Schwarz
The Lancet | ELSEVIER SCIENCE INC | Published : 2015
Grants
Funding Acknowledgements
German Ministry of Education and Research; Orphatec/Colbourne Pharmaceuticals.