Journal article

Therapy Development for the Lysosomal Storage Disease Fucosidosis using the Canine Animal Model

Jessica L Fletcher, Rosanne M Taylor

Pediatric Endocrinology Reviews | MEDICAL MEDIA | Published : 2016

University of Melbourne Researchers

Grants

Awarded by NCRR NIH HHS

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Keywords

Globoid-Cell Leukodystrophy
Inherited Metabolic Disease
Twitcher Mice
Gene-Transfer
Lysosomal Storage Disease
Enzyme-Replacement-Therapy
Science & Technology
Neuronal Ceroid-Lipofuscinosis
Alpha-L-Fucosidase
Combined Modality Therapy
Fucosidosis
Inherited Metabolic-Disorders
Brain
Animals
Enzyme Replacement Therapy
Genetic Therapy
Hematopoietic Cell Transplantation
Canine Fucosidosis
Bone-Marrow-Transplantation
Life Sciences & Biomedicine
Springer-Spaniels
Dogs
Humans
Glycoproteinoses
Mouse Model
Disease Models, Animal
Endocrinology & Metabolism
Hematopoietic Stem Cell Transplantation