Journal article

Challenges of diagnostic exome sequencing in an inbred founder population

DN Azmanov, T Chamova, R Tankard, V Gelev, M Bynevelt, L Florez, D Tzoneva, D Zlatareva, V Guergueltcheva, M Bahlo, I Tournev, L Kalaydjieva

Molecular Genetics and Genomic Medicine | WILEY | Published : 2013

Open access

Abstract

Exome sequencing was used as a diagnostic tool in a Roma/Gypsy family with three subjects (one deceased) affected by lissencephaly with cerebellar hypoplasia (LCH), a clinically and genetically heterogeneous diagnostic category. Data analysis identified high levels of unreported inbreeding, with multiple rare/novel “deleterious” variants occurring in the homozygous state in the affected individuals. Step-wise filtering was facilitated by the inclusion of parental samples in the analysis and the availability of ethnically matched control exome data. We identified a novel mutation, p.Asp487Tyr, in the VLDLR gene involved in the Reelin developmental pathway and associated with a rare form of LC..

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University of Melbourne Researchers

Grants

Awarded by NHMRC Training Fellowship


Awarded by Australian Research Council Future Fellowship


Awarded by NHMRC Program


Funding Acknowledgements

We are grateful to the affected family and control individuals participating in this study. D. N. A. is supported by NHMRC Training Fellowship 634551. The study of D. N. A., L. F., and L. K. is supported by Medical and Health Research Infrastructure Fund, Western Australia and by the Western Australian Institute for Medical Research. M. B. is supported by Australian Research Council Future Fellowship FT100100764 and NHMRC Program Grant 490037. The study of M. B. and R. T. is supported by Victorian State Government Operational Infrastructure Support and the Australian Government NHMRC Independent Research Institute Infrastructure Support Scheme.