Oral pharmacological chaperone migalastat compared with enzyme replacement therapy in Fabry disease: 18-month results from the randomised phase III ATTRACT study
Derralynn A Hughes, Kathleen Nicholls, Suma P Shankar, Gere Sunder-Plassmann, David Koeller, Khan Nedd, Gerard Vockley, Takashi Hamazaki, Robin Lachmann, Toya Ohashi, Iacopo Olivotto, Norio Sakai, Patrick Deegan, David Dimmock, Francois Eyskens, Dominique P Germain, Ozlem Goker-Alpan, Eric Hachulla, Ana Jovanovic, Charles M Lourenco Show all
Journal of Medical Genetics | BMJ PUBLISHING GROUP | Published : 2017
Awarded by Novo Nordisk Fonden
Awarded by Grants-in-Aid for Scientific Research
Funding Amicus Therapeutics, Cranbury, NJ, USA.