Dystrophin Delivery to Muscles of mdx Mice Using Lentiviral Vectors Leads to Myogenic Progenitor Targeting and Stable Gene Expression
En Kimura, Sheng Li, Paul Gregorevic, Brent M Fall, Jeffrey S Chamberlain
Molecular Therapy | CELL PRESS | Published : 2010
We thank Arthur Thompson for reviewing this manuscript and Laura Stewart for her help with the Bethesda assay. We are grateful to Rita Sarker for providing the hemophilic mice. We also thank Baxter Biosciences for providing the rhFVIII (Advate). This work was supported by grant funding from the Hemophilia Association of New York and a Judith Graham Pool Postdoctoral Fellowship award to Rui-Jun Su. The authors have no competing financial interests. R. S. designed and performed research, analyzed data, and wrote the manuscript. A. E. performed research. Y. L. designed research and analyzed data. D. B. analyzed data. S. W. P. provided reagents and designed research. N. C. J. designed research, analyzed data, and wrote the manuscript.