Journal article

Antisense oligonucleotide modified with serinol nucleic acid (SNA) induces exon skipping in: Mdx myotubes

BT Le, K Murayama, F Shabanpoor, H Asanuma, RN Veedu

RSC Advances | Published : 2017

Abstract

We investigated the potential of SNA-modified antisense oligonucleotide (AO) for exon-skipping. We found that a 20-mer SNA-AO induced efficient exon-23 skipping in the mouse dystrophin gene transcript.

University of Melbourne Researchers

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