Journal article
Safety of switching to Migalastat from enzyme replacement therapy in Fabry disease: Experience from the Phase 3 ATTRACT study
DA Hughes, K Nicholls, G Sunder-Plassmann, A Jovanovic, U Feldt-Rasmussen, R Schiffmann, R Giugliani, V Jain, C Viereck, JP Castelli, N Skuban, JA Barth, DG Bichet
American Journal of Medical Genetics Part A | WILEY | Published : 2019
DOI: 10.1002/ajmg.a.61105
Grants
Funding Acknowledgements
Amicus Therapeutics, Inc.