Journal article
Neuronal Ceroid Lipofuscinosis type 2: an Australian case series
Alexandra M Johnson, Simone Mandelstam, Ian Andrews, Katja Boysen, Joy Yaplito-Lee, Michael Fietz, Lakshmi Nagarajan, Victoria Rodriguez-Casero, Monique M Ryan, Nicholas Smith, Ingrid E Scheffer, Carolyn Ellaway
Journal of Paediatrics and Child Health | WILEY | Published : 2020
DOI: 10.1111/jpc.14890
Grants
Funding Acknowledgements
Writing support was provided by Emma Conran, Porterhouse Medical, Reading, UK, and funded by BioMarin Pharmaceutical Inc.