Journal article

Trial of Deferiprone in Parkinson's Disease

D Devos, J Labreuche, O Rascol, JC Corvol, A Duhamel, PG Delannoy, W Poewe, Y Compta, N Pavese, E Ruzička, P Dušek, B Post, BR Bloem, D Berg, W Maetzler, M Otto, MO Habert, S Lehericy, J Ferreira, R Dodel Show all

New England Journal of Medicine | Published : 2022

Abstract

Background Iron content is increased in the substantia nigra of persons with Parkinson's disease and may contribute to the pathophysiology of the disorder. Early research suggests that the iron chelator deferiprone can reduce nigrostriatal iron content in persons with Parkinson's disease, but its effects on disease progression are unclear. Methods We conducted a multicenter, phase 2, randomized, double-blind trial involving participants with newly diagnosed Parkinson's disease who had never received levodopa. Participants were assigned (in a 1:1 ratio) to receive oral deferiprone at a dose of 15 mg per kilogram of body weight twice daily or matched placebo for 36 weeks. Dopaminergic therapy ..

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University of Melbourne Researchers