Gene induction for the treatment of methylmalonic aciduria
Ruimei Hu, Nicole E Buck, Mahmoud S Khaniani, Leonie Wood, Hady Wardan, Jean-Francois Benoist, Lingli Li, Jim Vadolas, Joseph P Sarsero, Panos A Ioannou, Heidi L Peters
Journal of Gene Medicine | WILEY | Published : 2009
Panos Ioannou passed away in April 2005. The authors wish to thank Dr Matthew Burton for flow cytometry assistance. This work was supported by funding from the Murdoch Childrens Research Institute. H.L.P. is the recipient of an NHRMC Clinical Career Development Award.