Conference Proceedings
Miglustat in Niemann-Pick disease type c (NPC)
Ed Wraith, Darleen Vecchio, Helena Prady, Larry Abel, Marc Patterson
MOLECULAR GENETICS AND METABOLISM | ACADEMIC PRESS INC ELSEVIER SCIENCE | Published : 2008
Conference Proceedings
Ed Wraith, Darleen Vecchio, Helena Prady, Larry Abel, Marc Patterson
MOLECULAR GENETICS AND METABOLISM | ACADEMIC PRESS INC ELSEVIER SCIENCE | Published : 2008