Journal article

Deferiprone in Friedreich Ataxia: A 6-Month Randomized Controlled Trial

Massimo Pandolfo, Javier Arpa, Martin B Delatycki, Kim Hanh Le Quan Sang, Caterina Mariotti, Arnold Munnich, Irene Sanz-Gallego, Geneieve Tai, Mark A Tarnopolsky, Franco Taroni, Michael Spino, Fernando Tricta

Annals of Neurology | WILEY | Published : 2014

DOI: 10.1002/ana.24248

Grants

Funding Acknowledgements

This study was funded by ApoPharma.

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Keywords

Humans
Iron Chelating Agents
Features
Severity of Illness Index
Deficiency
Disease
Friedreich Ataxia
Iron
Female
Dose-Response Relationship, Drug
Male
Life Sciences & Biomedicine
Chelation
Disability Evaluation
Neurosciences
Double-Blind Method
Deferiprone
Electrocardiography
Neurosciences & Neurology
Child
Treatment Outcome
Ventricular Function, Left
Clinical Neurology
Adolescent
Frataxin
Aconitase
Rating-Scale
Placebo-Controlled Trial
Idebenone
Adult
Young Adult
Pyridones
Science & Technology